Mohammed A. Rafi

Mohammed A. Rafi,

Contact Dr. Rafi

1020 Locust Street
Suite 393 JAH
Philadelphia, PA 19107

(215) 503-5715
(215) 923-7747 fax

Most Recent Peer-reviewed Publications

  1. Targeted enzyme delivery systems in lysosomal disorders: an innovative form of therapy for mucopolysaccharidosis
  2. Peptide-mediated drug delivery across the blood-brain barrier for targeting brain tumors
  3. AAVrh10 Gene Therapy Ameliorates Central and Peripheral Nervous System Disease in Canine Globoid Cell Leukodystrophy (Krabbe Disease)
  4. Recent advances in targeted delivery of tissue plasminogen activator for enhanced thrombolysis in ischaemic stroke
  5. Enzyme replacement therapies: What is the best option?
  6. Spectrophotometric analysis of thrombolytic activity: SATA assay
  7. Debate on human aging and lifespan
  8. Krabbe disease: One Hundred years from the bedside to the bench to the bedside
  9. Gene therapy for CNS diseases - Krabbe disease
  10. Blood-brain barrier transport machineries and targeted therapy of brain diseases
  11. Long-term improvements in lifespan and pathology in CNS and PNS after BMT plus one intravenous injection of AAVrh10-GALC in twitcher mice
  12. To impact or not to impact, this is not a question for BioImpacts!
  13. A prospective highlight on exosomal nanoshuttles and cancer immunotherapy and vaccination
  14. Intravenous injection of AAVrh10-GALC after the neonatal period in twitcher mice results in significant expression in the central and peripheral nervous systems and improvement of clinical features
  15. Krabbe disease: Are certain mutations disease-causing only when specific polymorphisms are present or when inherited in trans with specific second mutations?
  16. Lysosomal storage diseases: Heterogeneous group of disorders
  17. Sixteen novel mutations in the arylsulfatase A gene causing metachromatic leukodystrophy
  18. Extended normal life after AAVrh10-mediated gene therapy in the mouse model of krabbe disease
  19. Gene and stem cell therapy: Alone or in combination?
  20. Combined effects of hyperglycemic conditions and HIV-1 Nef: A potential model for induced HIV neuropathogenesis